In getting ready for the day, columnist Connie Chandler's caregiver helps her look good on the outside, but Connie's attitude ...

The arrival of a new night weekend nurse has given columnist Ari Anderson reason to believe that he's now on the path of ...

Scholar Rock is once again seeking approval in Europe for its muscle-strengthening drug for SMA, already launching in the U.S. as Isembyld.

Columnist Sherry Toh may be waiting to try Isembyld, but the new SMA treatment should still be made accessible quickly, she ...

England has launched SMA newborn screening in the West Midlands, marking the first step toward a nationwide NHS rollout.

Columnist Connie Chandler recalls a trip she took to the Rocky Mountains, and how the challenges were a call to go further up ...

A compound in some fruits may be a treatment candidate for SMA, according to a study that explored the effects of autophagy ...

For many people living with rare neuromuscular diseases, the most meaningful part of a recent Chicago gathering was not just the medical updates — it was finding a community that understood their ...

There are several treatment options available for spinal muscular atrophy (SMA), a rare genetic condition characterized by progressive muscle weakness and wasting. The disease mainly affects motor ...

« MDA Toast to Life Gala – Orlando, FL 2026 Puerto Rico Muscle Walk » ...

Recognized as the leading international meeting dedicated to neuromuscular diseases, the conference convenes renowned researchers, clinicians, affiliated health care providers, academicians, advocates ...