Roche and PTC Therapeutics' Evrysdi for spinal muscular atrophy (SMA) has been approved by the FDA for younger children with the rare disease, extending its use to include infants less than two months ...
Unresolved compliance issues at a manufacturing plant operated by Novo Nordisk have led to a complete response letter for Scholar Rock's lead drug for spinal muscular atrophy (SMA). The CRL is related ...
Unified managed accounts (UMAs) and separately managed accounts (SMAs) are two account types that offer high-net-worth clients more control and flexibility than mutual funds. Both options let you ...
SMA Solar Technology AG said its Sunny Central Storage battery inverter has become the first system in Germany to receive a unit certificate for grid-forming mode with instantaneous reserve. The ...
SMA management expects negative one-time losses between €170-220 million. Image: SMA Solar. SMA Solar has forecast financial losses and further restructuring measures in 2025, as it responds to ...
Continuous, previously SMA Technologies, offers integrated automation, intelligent document processing, and information security tools for banks and credit unions to serve critical banking functions ...
Risdiplam, an oral pre–messenger RNA splicing modifier, is an efficacious treatment for persons with symptomatic spinal muscular atrophy (SMA). The safety and efficacy of risdiplam in presymptomatic ...
Chester was eight months old when his parents were finally told the condition that meant he couldn't swallow or move his legs and left him constantly distressed was spinal muscular atrophy, or SMA.
PICTURES OUT FRONT. NEW AT FIVE FLORIDA FACES A MAJOR SHORTAGE OF PSYCHIATRISTS, RANKING AMONG THE WORST STATES IN THE NATION. BUT ONE FLORIDA CENTRAL FLORIDA BEHAVIORAL HEALTH CARE PROVIDER HOPES TO ...
In addition to all of the creative superlatives we can lay on It’s Always Sunny in Philadelphia as it approaches the 20th anniversary of its debut in August, the FX comedy has provided perhaps the ...
CREDIT: Friends of Big Bear Valley. Get the Popular Science daily newsletter💡 Breakthroughs, discoveries, and DIY tips sent every weekday. Terms of Service and ...
Megan Molteni reports on discoveries from the frontiers of genomic medicine, neuroscience, and reproductive tech. She joined STAT in 2021 after covering health and science at WIRED. You can reach ...
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